Huntington’s disease is a rare inherited neurological disorder that progressively affects movement, cognition and mental ...
Experimental gene therapies like AMT‑130 lower toxic huntingtin protein and significantly slow Huntington’s disease, offering ...
In a groundbreaking first, a gene therapy in clinical trials has slowed the progression of Huntington's disease, a rare genetic disorder in which toxic bits of protein cause brain cells to malfunction ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today announced that ...
Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...
Huntington's disease is caused by an inherited genetic change that causes production of an altered protein. This leads to nerve damage in areas of the brain that control movement and thinking.
Huntington’s disease (HD) is one of those rare conditions that affects not just the patient but the entire family—medically, emotionally and genetically. This inherited brain disorder causes gradual ...
TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...
Medically reviewed by Smita Patel, DO Key Takeaways Genetic testing is the definitive diagnostic tool to identify the gene that causes Huntington’s disease, and you can have the genetic test years ...
Symptoms caused by Huntington's disease include loss of motor control, involuntary movements, dementia, mood disorders, and psychiatric though disturbances.
Huntington's disease (HD) has long been impossible to cure, but new research is finally giving fresh hope. HD is a progressive, hereditary brain disease that affects movement, cognition and emotions.
Synaptic plasticity - the brain's ability to modify the connections between neurons to support learning - is one of the neural functions profoundly altered in Huntington's disease, with a direct ...